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Rare Disease
Patient Access
Rare Disease Day Highlights a Research Gap
March 2, 2026
Blog
Patient Access
Rare Disease Support Means Protecting Treatment Access
February 25, 2026
Blog
Patient Access
Rare Disease Patients Share Common Challenges
February 23, 2026
Blog
Patient Access
Newborns Will Now Be Tested for Two More Rare Conditions
February 18, 2026
Blog
Patient Access
Protecting a Lifeline for Pediatric Rare Disease Research
January 22, 2026
Blog
Patient Access
Congress Weighs Proposal to Cure Hep C
December 17, 2025
Blog
Patient Access
ASAP Act Would Expand Alzheimer’s Detection
November 21, 2025
Blog
Health Technology Assessment
When AI Oversteps in Medical Care
October 27, 2025
Blog
Patient Access
Two New Diseases Could Be Added to Infant Screening Panel
September 3, 2025
Blog
Infant
Shuttering Screening Committee Puts Babies at Risk
May 21, 2025
Blog
Patient Access
White House Thrusts Drug Pricing Back into the Spotlight
May 16, 2025
Blog
Patient Access
A Landmark Law Turns 15
May 2, 2025
Blog
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